Results of a Global Phase 3, Randomized, Double-Blind, Placebo-Controlled Trial Evaluating the Efficacy and Safety of Sebelipase Alfa as an Enzyme Replacement Therapy in Children and Adults with Lysosomal Acid Lipase Deficiency


Balwani M., Burton B., Baric I., Bialer M., Burrow T. A. , Camarena Grande C., ...More

HEPATOLOGY, vol.60, no.6, 2014 (Journal Indexed in SCI) identifier

  • Publication Type: Article / Abstract
  • Volume: 60 Issue: 6
  • Publication Date: 2014
  • Title of Journal : HEPATOLOGY