A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency


Burton B. K. , BALWANİ M., FEİLLET F., BARİC I., Burrow T. A. , CAMARENA GRANDE C., ...More

NEW ENGLAND JOURNAL OF MEDICINE, vol.373, no.11, pp.1010-1020, 2015 (Journal Indexed in SCI) identifier identifier identifier

  • Publication Type: Article / Article
  • Volume: 373 Issue: 11
  • Publication Date: 2015
  • Doi Number: 10.1056/nejmoa1501365
  • Title of Journal : NEW ENGLAND JOURNAL OF MEDICINE
  • Page Numbers: pp.1010-1020

Abstract

BACKGROUND